This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...

A genetic medicine at the heart of a $387 million Kyowa Kirin acquisition has won FDA approval, a regulatory decision that makes the one-time treatment the first approved therapy for the rare ...

Preparations are underway by Kyowa Kirin to begin a study in Japan for the therapy targeting children with PSEJ Japan's Ministry of Health, Labor and Welfare (MHLW) has granted orphan regenerative ...

Dublin, March 10, 2026 (GLOBE NEWSWIRE) -- The "Libmeldy Market Report 2026: Epidemiology, Pipeline Analysis, Market Insights & Forecasts" has been added to ResearchAndMarkets.com's offering. The ...

(RTTNews) - The U.S. Food and Drug Administration approved Lenmeldy (atidarsagene autotemcel) gene therapy to treat children with early-onset metachromatic leukodystrophy or MLD. Lenmeldy, formerly ...

The US Food and Drug Administration (FDA) has approved the first gene therapy for metachromatic leukodystrophy (MLD), a rare and debilitating genetic disease affecting the brain and nervous system.

Share on Pinterest Scientists have managed to create a treatment for the rare genetic disorder MLD. smolaw11/Getty Images Doctors in the United Kingdom have used a revolutionary gene therapy to cure a ...

Shares of Orchard Therapeutics (ORTX) have lost a whopping 96% of their value since my initial foray into this gene therapy pioneer in 2019. Over the last year, they've lost roughly a third of their ...

BEDFORD, Mass., Feb. 22, 2023 (GLOBE NEWSWIRE) -- Homology Medicines, Inc. (Nasdaq: FIXX), a genetic medicines company, announced today the presentation of preclinical data that supports the targeted, ...