Sarepta Therapeutics, Inc. (SRPT) was founded in 1980 and is based in Cambridge, Massachusetts. The company is focused on developing RNA-based therapeutics and gene therapy against Duchenne muscular ...
Dyne Therapeutics, Inc. (DYN) is advancing the use of its FORCE platform to target skeletal muscle disorders. This would be with the use of modern oligonucleotide technology drugs like DYNE-101 and ...
- BridgeBio will also share 15-month Phase 2 data and review the Phase 3 clinical trial design of BBP-418, a potential therapeutic for patients with LGMD2I, with initiation of its Phase 3 study ...