Sarepta Therapeutics, Inc. (SRPT) was founded in 1980 and is based in Cambridge, Massachusetts. The company is focused on developing RNA-based therapeutics and gene therapy against Duchenne muscular ...
Mean muscle content-adjusted dystrophin expression of 9.0% and unadjusted dystrophin of 5.5%, with high consistency across participants, in a prespecified analysis; dystrophin was comprised of two ...